3 Patents
- US122905742025Optimized Promoter Sequences, Intron-free Expression Constructs and Methods of Use
Spark Therapeutics, Inc.
0 cites - US120846932024Codon-optimized Acid Alpha-glucosidase Expression Cassettes and Methods of Using Same
SPARK THERAPEUTICS, Inc.
0 cites - US118966522024Modified Factor IX, and Compositions, Methods and Uses for Gene Transfer to Cells, Organs, and Tissues
The Children's Hospital Of Philadelphia
0 cites