7 Patents
- US123919472025Modulation of SPTLC1 via Recombinant Adeno-associated Vectors
University Of Massachusetts
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- US121631292024Antisense Oligonucleotides to Restore Dysferlin Protein Expression in Dysferlinopathy Patient Cells
University Of Massachusetts
0 cites - US118278862023Compositions and Methods for Modulating Dysferlin Expression
University Of Massachusetts
0 cites - US117609992023Raav-based Compositions and Methods for Treating Amyotrophic Lateral Sclerosis
University Of Massachusetts
0 cites - 0 cites