6 Patents
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- US119639752024Therapeutic Targets for Facioscapulohumeral Muscular Dystrophy
University Of Massachusetts
0 cites - US118734942024Genetic and Pharmacological Transcriptional Upregulation of the Repressed FXN Gene as a Therapeutic Strategy for Friedreich Ataxia
University Of Massachusetts
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- US116802752023Self-regulating AAV Vectors for Safe Expression of Mecp2 in Rett Syndrome
University Of Massachusetts
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