30 Patents
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- US124912352025Methods and Compositions for Treating Metabolic Imbalance in Neurodegenerative Disease
University Of Massachusetts
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- US124670632025Recombinant AAV Vectors Useful for Reducing Immunity Against Transgene Products
University Of Massachusetts
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- US123983782025Aav-mediated Gene Therapy for Maple Syrup Urine Disease (MSUD)
The Clinic For Special Children, Inc.
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- US121957672025Adeno-associated Virus Gene Therapy for 21-hydroxylase Deficiency
Adrenas Therapeutics, Inc.
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- US119268422024Use of Inverted Terminal Repeats (ITRS) from Adeno-associated Virus Serotypes 8 and RH.39 in Gene Therapy Vectors
University Of Massachusetts
0 cites - US119201682024Compositions and Methods for Transient Delivery of Nucleases
University Of Massachusetts
0 cites - US118828152024Recombinant Adeno-associated Viruses for Delivering Gene Editing Molecules to Embryonic Cells
University Of Massachusetts
0 cites - US118516572023Anti-angiogenic Mirna Therapeutics for Inhibiting Corneal Neovascularization
University Of Massachusetts
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- US117734102023Repairing Compound Heterozygous Recessive Mutations by Allele Exchange
University Of Massachusetts
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- US116802742023Method of Increasing the Function of an AAV Vector
The Trustees Of The University Of Pennsylvania
0 cites - US116802752023Self-regulating AAV Vectors for Safe Expression of Mecp2 in Rett Syndrome
University Of Massachusetts
0 cites - US116741542023Gene Therapeutics for Fibrodysplasia Ossificans Progressiva
University Of Massachusetts
0 cites - US116554832023Use of Novel Mirna-binding Site Cassettes for Antigen-presenting Cell Detargeting of Transgene Expression by Raav Gene Therapy Vectors
University Of Massachusetts
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