- US12595469utility2026Treatment of Retinitis Pigmentosa Using Improved Engineered Meganucleases0 cites
- US12595470utility2026Engineered Nucleases That Target Human and Canine Factor VIII Genes as a Treatment for Hemophilia A0 cites
- US12448613utility2025Genetically-modified T Cells Comprising a Modified Intron in the T Cell Receptor Alpha Gene0 cites
- US12410418utility2025Optimized Engineered Meganucleases Having Specificity for a Recognition Sequence in the Hepatitis B Virus Genome0 cites
- US12351839utility2025Rationally-designed Single-chain Meganucleases with Non-palindromic Recognition Sequences0 cites
- US11866747utility2024Engineered Meganucleases That Target Human Mitochondrial Genomes0 cites
- US11851680utility2023Genetically-modified Immune Cells Comprising a Microrna-adapted Shrna (shrnamir)0 cites
- US11786554utility2023Optimized Engineered Nucleases Having Specificity for the Human T Cell Receptor Alpha Constant Region Gene0 cites
- US11680254utility2023Engineered Meganucleases Specific for Recognition Sequences in the PCSK9 Gene0 cites